
Tag: gene therapy


CRISPR baby mutation significantly increases mortality: Two copies of mutated CCR5 gene associated with lower survivability

Geneticists continue to unravel how genes impact drug use and addiction: Study assesses naturally occurring variation in drug self-administration

Insulin under the influence of light

New immunodeficiency disease discovered: Scientists find the answer in a single gene mutation

Researchers ready B cells for novel cell therapy

Working to advance radiation therapy for children with cancer: Novel software to improve accuracy of cancer treatment

How light triggers brain activity: Protein research

High-speed ‘electron camera’ films molecular movie in HD

Novel strategy hits ‘reset button’ for disease-causing genetic duplications

Unjamming the genome after DNA damage: A gene regulatory multi-tool has yet another function

New protein for gene editing may improve disease treatment, sustainable manufacturing: Innovation could change how gene editing is approached in the future

New muscular disease: Myoglobinopathy

Using more-specific ‘genetic scissors’ may avoid problems associated with gene editing

Robust and specific gene regulation tool developed for primary brain neurons

How a certain bacterium communicates and makes us sick

Identical twins light the way for new genetic cause of arthritis

New device widens light beams by 400 times: Broadening possibilities in science and technology

DNA structure impacts rate and accuracy of DNA synthesis

Preventing sudden cardiac death with genome editing

Studies raise questions over how epigenetic information is inherited

Making gene therapy delivery safer and more efficient: Inconsistency in the molecular makeup of vectors is a key concern in scaling up gene therapy production for patients

How many people carry rare disease genetic risk variants?

How bacteria play pass the parcel — and help each other evade antibiotics

A first step toward cracking the genetics of strabismus: A mysterious variant on chromosome 21, in patients with esotropia, is the first to be linked to common strabismus

How to make the gene-editing tool CRISPR work even better

Mutation ‘hotspots’ in DNA: Research could lead to new insights on cancer risks

Mutated gene is likely cause of 3-year-old girl’s severe disorder: Damaged gene FBXO28

Imaging in living cells reveals how ‘junk DNA’ switches on a gene: Video shows DNA enhancers finding and activating a target gene in a living cell
